Beam Therapeutics has provided a much-awaited update on its therapy that uses a form of CRISPR called base editing to precisely fix a single genetic typo...
Boehringer Ingelheim plans for dealmaking and R&D spending amid US price pressure
Long-awaited results from Phase 1/2 studies lifted Sarepta’s stock and, according to the company, suggest potential for two medicines to treat muscle-weakening conditions.
During a gathering of Massachusetts political and company officials earlier this week, Rentschler Biopharma, a CDMO headquartered in Laupheim, Germany, cited the continued evolution and progress...
This year’s catalysts in the space include a near-term FDA decision on Eli Lilly’s oral challenger to the new Wegovy pill. Looking further ahead, Novo Nordisk...
Novo reports more triple-G data from China; Grifols plots IPO for biopharma unit
Sarepta Therapeutics’ next crop of medicines for muscular dystrophy appear to be safe and effective in early clinical trials, the company said, a positive though incremental...
The FDA has approved Denali Therapeutics’ enzyme replacement therapy for a genetic lysosomal storage disease after a string of high-profile rejections for rare disease candidates.
The Belgian drugmaker plans to hire about 330 people at a facility that will use advanced manufacturing technologies including AI, robotics and automation to meet rising...
Billion dollar-backed AI drug developer, Xaira Therapeutics, has recently released the largest virtual cell model to-date to predict how cells respond to genetic perturbations in unseen biological contexts. The team asserts that accurately predicting transcriptome-level effects is a...